X Chromosome Treatments: Advancements for Genetic Disorders

April 7, 2025

X chromosome treatments are emerging as a groundbreaking approach in the fight against various genetic disorders, particularly those linked to the X chromosome such as Fragile X Syndrome and Rett Syndrome.The complexity of X chromosome inactivation, a process crucial for managing gene dosage in females, has captivated researchers for decades, and recent discoveries are paving the way for innovative therapies.
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